CI

At a glance

ClinicalIndex Comparison Record
Phase 4Completed· 67 enrolled
Drug / intervention
agalsidase betabiological
Likely dose
agalsidase beta 1.0 mg/kg intravenously every 2 weeksAI-extracted
Key inclusion· 1
  • Successfully completed the prior double-blind AGAL-008-00 study (NCT00074984)
Key exclusion· 4
  • Unable to complete the prior AGAL-008-00 study
  • History of kidney transplantation or currently on dialysis
  • Diabetes mellitus or confounding renal disease
  • Clinically significant organic disease or unstable medical condition precluding participation

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT00081497
NCT00081497Phase 4Completed

Multi-Center, Open-Label Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease That Previously Participated in the AGAL-008-00 Study

Genzyme, a Sanofi Company·interventional·Posted Apr 16, 2004·Updated Apr 2, 2015

In Brief

A Phase 4 clinical trial evaluating agalsidase beta for Fabry Disease. Completed, enrolled 67 participants across 25 sites in 6 countries.

Detailed Summary

People with Fabry Disease have an alteration in their genetic material (DNA) which causes a deficiency of the alpha-galactosidase A enzyme. Fabrazyme (agalsidase beta) is a drug that helps to break down and removes certain types of fatty substances called "glycolipids". These glycolipids are normally present within the body in most cells. In Fabry disease, glycolipids build up in various tissues such as the liver, kidney, skin, and blood vessels because a-galactosidase A is not present, or is present in small quantities. The build up of glycolipid (globatriaosylceramide or GL-3) levels in these tissues in particular is thought to cause the clinical symptoms that are common to Fabry disease. This study analyzed the safety and efficacy of Fabrazyme in the treatment of patients with Fabry disease that previously participated in the AGAL-008-00 (NCT0074984) study.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsFabry Disease
CountriesCanada, Czechia, Hungary, Poland, United Kingdom, United States
Collaborators--

Timeline

Phase 4CompletedFinished
200420052006200720082009201020112012201320142015201620172018201920202021202220232024202520262027
First PostedApr 16, 2004
Enrollment StartJan 1, 2004
Primary CompletionSep 1, 2005
TodayJul 2, 2026
Enrollment to primary: 1.7 yearsPosted 22.2 years ago

Interventions

agalsidase betabiological

1.0 mg/kg every 2 weeks