At a glance
ClinicalIndex Comparison RecordPhase 1Completed· 22 enrolled
Drug / intervention
Unrelated Umbilical Cord Blood Transplant +1 morebiological
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.
Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.
A Pilot Study of Reduced Intensity Conditioning in Pediatric Patients <21 Years of Age With Non-Malignant Disorders Undergoing Umbilical Cord Blood Transplantation
In Brief
A Phase 1 clinical trial evaluating Unrelated Umbilical Cord Blood Transplant and Reduced Intensity Conditioning for Non Malignant Disorders and 7 related conditions. Completed, enrolled 22 participants across 1 site.
Detailed Summary
The primary objective is to determine the feasibility of attaining acceptable rates of donor cell engraftment (\>25% donor chimerism at 180 days) following reduced intensity conditioning (RIC) regimens in pediatric patients \< 21 years receiving cord blood transplantation for non-malignant disorders.
Study Details
Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsNon Malignant Disorders, Immunodeficiencies, Congenital Marrow Failures, Hemoglobinopathies, Inborn Errors of Metabolism, Sickle Cell, Thalassemia, Lysosomal Storage Disease
CountriesUnited States
Collaborators--
Timeline
Phase 1CompletedFinished
200920102011201220132014201520162017201820192020202120222023202420252026
First PostedSep 2008
Enrollment StartOct 2008
Primary CompletionDec 2012
Study CompletionApr 2014
TodayJul 2026
First PostedSep 1, 2008
Enrollment StartOct 1, 2008
Primary CompletionDec 1, 2012
Study CompletionApr 1, 2014
TodayJul 2, 2026
Enrollment to primary: 4.2 yearsPosted 17.8 years ago
Interventions
Unrelated Umbilical Cord Blood Transplantbiological
Reduced Intensity Conditioning for unrelated umbilical cord blood transplant
Reduced Intensity Conditioningdrug