CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 18 enrolled
Drug / intervention
PRO044 SC +1 moredrug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT01037309
NCT01037309Phase 2Completed

A Phase I/IIa, Open Label, Escalating Dose, Pilot Study to Assess the Effect, Safety, Tolerability and Pharmacokinetics of Multiple Subcutaneous and Intravenous Doses of PRO044 in Patients With Duchenne Muscular Dystrophy

BioMarin Pharmaceutical·interventional·Posted Dec 23, 2009·Updated Oct 16, 2018

In Brief

A Phase 2 clinical trial evaluating PRO044 SC and PRO044 IV for Duchenne Muscular Dystrophy. Completed, enrolled 18 participants across 4 sites in 4 countries.

Detailed Summary

The purpose of this study is to see whether PRO044 is safe and effective to use as medication for DMD patients with a mutation around location 44 in the DNA for the dystrophin protein.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesBelgium, Italy, Netherlands, Sweden
Collaborators--

Timeline

Phase 2CompletedFinished
20102011201220132014201520162017201820192020202120222023202420252026
First PostedDec 23, 2009
Enrollment StartDec 1, 2009
Primary CompletionMay 1, 2013
Study CompletionOct 1, 2013
TodayJul 2, 2026
Enrollment to primary: 3.4 yearsPosted 16.5 years ago

Interventions

PRO044 SCdrug

Subcutaneous injection, once a week, for five weeks

PRO044 IVdrug

Intravenous injection, once a week, for five weeks