At a glance
ClinicalIndex Comparison RecordPhase 2Completed· 17 enrolled
Drug / intervention
Clenbuterol +1 moredrug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.
Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.
A Clinical Investigation of the Safety and Efficacy of Clenbuterol on Motor Function in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy
In Brief
A Phase 2 clinical trial evaluating Clenbuterol and Placebo for Pompe Disease. Completed, enrolled 17 participants across 1 site.
Detailed Summary
Funding Source- FDA OOPD The purpose of this study is to investigate the safety and efficacy of clenbuterol on motor function in individuals with late-onset Pompe disease (LOPD) who are treated with enzyme replacement therapy (ERT).
Study Details
Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsPompe Disease
CountriesUnited States
Collaborators--
Timeline
Phase 2CompletedFinished
2014201520162017201820192020202120222023202420252026
Enrollment StartSep 2013
First PostedSep 2013
Primary CompletionSep 2016
TodayJul 2026
First PostedSep 16, 2013
Enrollment StartSep 1, 2013
Primary CompletionSep 2, 2016
TodayJul 2, 2026
Enrollment to primary: 3.0 yearsPosted 12.8 years ago
Interventions
Clenbuteroldrug
Placebodrug