At a glance
ClinicalIndex Comparison RecordStandardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.
Patient Registry of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS)
In Brief
An observational study for Friedreich's Ataxia. Completed, enrolled 1,200 participants across 16 sites in 10 countries.
Detailed Summary
This is a multi-centre, multi-national, prospective, observational study of Friedreich's Ataxia (FRDA) with a control group to: * obtain natural history data on individuals affected by FRDA * relate clinical assessments and results from proteomic analyses * expedite identification and recruitment of participants for clinical trials * develop and validate sensitive and reliable outcome measures for detecting onset and change over the natural course of FRDA which may also be potential outcome measures for use in future clinical trials and clinical care * plan for future research studies