CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 15 enrolled
Drug / intervention
AAV2-hCHMbiological
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT02341807
NCT02341807Phase 2Completed

A Phase 1/2 Safety Study in Subjects With CHM (Choroideremia) Gene Mutations Using an Adeno-Associated Virus Serotype 2 Vector to Deliver the Normal Human CHM Gene [AAV2-hCHM] to the Retina

Spark Therapeutics, Inc.·interventional·Posted Jan 19, 2015·Updated Jan 25, 2024

In Brief

A Phase 2 clinical trial evaluating AAV2-hCHM for Choroideremia and CHM (Choroideremia) Gene Mutations. Completed, enrolled 15 participants across 3 sites.

Detailed Summary

This clinical study evaluates the safety and tolerability of AAV2-hCHM in participants with Choroideremia gene mutations.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesUnited States
Collaborators--

Timeline

Phase 2CompletedFinished
201520162017201820192020202120222023202420252026
First PostedJan 19, 2015
Enrollment StartJan 15, 2015
Primary CompletionOct 12, 2022
TodayJul 2, 2026
Enrollment to primary: 7.7 yearsPosted 11.5 years ago

Interventions

AAV2-hCHMbiological

Comparison of different dosages of AAV2-hCHM