CI

At a glance

ClinicalIndex Comparison Record
Phase 2Active· 75 enrolled
Drug / intervention
Autologous Adipose-derived Mesenchymal Stromal Cellsdrug
Likely dose
Autologous Adipose-derived Mesenchymal Stromal Cells 10 mLfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT03268603
NCT03268603Phase 2Active

A Phase II Study of Intrathecal Autologous Adipose-derived Mesenchymal Stromal Cells for Amyotrophic Lateral Sclerosis

Mayo Clinic·interventional·Posted Aug 31, 2017·Updated Mar 9, 2026

In Brief

A Phase 2 clinical trial evaluating Autologous Adipose-derived Mesenchymal Stromal Cells for ALS and Amyotrophic Lateral Sclerosis. Active but no longer recruiting, targeting 75 participants across 3 sites.

Detailed Summary

The purpose of this study is to determine the safety and efficacy of intrathecal treatment delivered to the cerebrospinal fluid (CSF) of mesenchymal stem cells in ALS patients every 3 months for a total of 4 injections over 12 months. Mesenchymal stem cells (MSCs) are a type of stem cell that can be grown into a number of different kinds of cells. In this study, MSCs will be taken from the subject's body fat and grown. CSF is the fluid surrounding the spine. The use of mesenchymal stem cells is considered investigational, which means it has not been approved by the Food and Drug Administration (FDA) for routine clinical use. However, the FDA has allowed the use of mesenchymal stem cells in this research study.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesUnited States

Timeline

Phase 2Active
2018201920202021202220232024202520262027
First PostedAug 31, 2017
Enrollment StartOct 10, 2017
Primary CompletionJan 31, 2024
Study CompletionDec 31, 2026
TodayJul 2, 2026
Enrollment to primary: 6.3 yearsPosted 8.8 years ago

Interventions

Autologous Adipose-derived Mesenchymal Stromal Cellsdrug

The investigational product consists of autologous adipose-derived Mesenchymal Stromal Cells (MSCs), suspended in 5-10 mL Lactated Ringer's. The MSC are provided in a sterile syringe labelled with appropriate patient and product identifiers ready for intrathecal injection.