CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 12 enrolled
Drug / intervention
PP-001drug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT03634475
NCT03634475Phase 2Completed

A Safety Study of Intravitreal PP-001 in Patients With Chronic, Non-Infectious Uveitis Having Chronic Inflammation

Panoptes Pharma GmbH·interventional·Posted Aug 16, 2018·Updated Oct 9, 2024

In Brief

A Phase 2 clinical trial evaluating PP-001 for Non-infectious Uveitis. Completed, enrolled 12 participants across 9 sites in 5 countries.

Detailed Summary

In this study, PP-001 is assessed for safety and efficacy in patients diagnosed with non-infectious chronic uveitis. PP-001 is a novel small molecule that inhibits a specific enzyme (Dihydroorotate Dehydrogenase) and has shown pre-clinical efficacy in treatment of non-infectious uveitis. PP-001 will be administered to participants as a single intravitreal injection in ascending doses.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustria, Belgium, Germany, Netherlands, United Kingdom
Collaborators--

Timeline

Phase 2CompletedFinished
2017201820192020202120222023202420252026
First PostedAug 16, 2018
Enrollment StartJan 1, 2017
Primary CompletionNov 1, 2018
Study CompletionApr 1, 2019
TodayJul 2, 2026
Enrollment to primary: 1.8 yearsPosted 7.9 years ago

Interventions

PP-001drug

Drug - no placebo