CI

At a glance

ClinicalIndex Comparison Record
Phase 1Completed· 17 enrolled
Drug / intervention
Caffeine Citrate 5 mg/kg +1 moredrug
Likely dose
Caffeine Citrate 5 mg/kgfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT03913221
NCT03913221Phase 1Completed

Pharmacokinetics and Safety of Caffeine in Neonates With Hypoxic-Ischemic Encephalopathy

University of North Carolina, Chapel Hill·interventional·Posted Apr 12, 2019·Updated Mar 27, 2025

In Brief

A Phase 1 clinical trial evaluating Caffeine Citrate 5 mg/kg and Caffeine Citrate 10 mg/kg for Hypoxic-Ischemic Encephalopathy. Completed, enrolled 17 participants across 1 site.

Detailed Summary

Hypoxic-ischemic encephalopathy (HIE) due to perinatal asphyxia is common and often fatal. Therapeutic hypothermia reduces mortality and morbidity in infants with HIE. Even with the widespread use of therapeutic hypothermia, \~60% of infants with HIE die or have neurodevelopmental impairment. As a result, there is an urgent, unmet public health need to develop adjuvant therapies to improve survival and neurodevelopmental outcomes in this population. Caffeine may offer neuroprotection for infants with HIE by blocking adenosine receptors in the brain and reducing neuronal cell death. In animal models of HIE, caffeine reduces white matter brain injury. Drugs in the same class as caffeine (i.e., methylxanthines) have been shown to be protective against acute kidney injury in the setting of HIE. However, their safety and efficacy have not been studied in the setting of therapeutic hypothermia and their effect on neurological outcomes is not known. Since these drugs reduce injury to the kidney in infants with HIE, they may also reduce injury to the brain. This phase I study will evaluate the pharmacokinetics, safety, and preliminary effectiveness of caffeine as an adjuvant therapy to improve neurodevelopmental outcomes in infants with HIE.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesUnited States

Timeline

Phase 1CompletedFinished
2020202120222023202420252026
First PostedApr 12, 2019
Enrollment StartAug 14, 2019
Primary CompletionJan 1, 2023
Study CompletionDec 31, 2024
TodayJul 2, 2026
Enrollment to primary: 3.4 yearsPosted 7.2 years ago

Interventions

Caffeine Citrate 5 mg/kgdrug

Loading dose of caffeine 20 mg/kg IV followed by two daily doses of 5 mg/kg IV.

Caffeine Citrate 10 mg/kgdrug

Loading dose of caffeine 20 mg/kg IV followed by two daily doses of 10 mg/kg IV.