CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 57 enrolled
Drug / intervention
TransCon CNP +1 moredrug
Likely dose
TransCon CNP 3.9 mgfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04085523
NCT04085523Phase 2Completed

ACcomplisH: A Phase 2, Multicenter, Double-blind, Randomized, Placebo-controlled, Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Subcutaneous Doses of TransCon CNP Administered Once Weekly for 52 Weeks in Prepubertal Children With Achondroplasia Followed by an Open-Label Extension Period

Ascendis Pharma A/S·interventional·Posted Sep 11, 2019·Updated May 22, 2025

In Brief

A Phase 2 clinical trial evaluating TransCon CNP and Placebo for TransCon CNP for Achondroplasia. Completed, enrolled 57 participants across 15 sites in 8 countries.

Detailed Summary

The trial is a multicenter, double-blind, randomized, placebo-controlled, dose escalation trial of weekly TransCon CNP administered subcutaneously in prepubertal children 2 to 10 years old, inclusive, with Achondroplasia.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsAchondroplasia
CountriesAustralia, Austria, Denmark, Germany, Ireland, New Zealand, Portugal, United States
Collaborators--

Timeline

Phase 2CompletedFinished
2020202120222023202420252026
First PostedSep 11, 2019
Enrollment StartJun 24, 2020
Primary CompletionSep 27, 2022
Study CompletionOct 1, 2024
TodayJul 2, 2026
Enrollment to primary: 2.3 yearsPosted 6.8 years ago

Interventions

TransCon CNPdrug

TransCon CNP drug product is a lyophilized powder in a single-use vial containing either TransCon CNP 3.9 mg CNP-38/vial or TransCon CNP 0.80 mg CNP-38/vial. Prior to use, the lyophilized powder is reconstituted with sterile water for injection and administered by subcutaneous injection via syringe and needle.

Placebo for TransCon CNPdrug

Weekly subcutaneously injection of placebo.