CI

At a glance

ClinicalIndex Comparison Record
Phase 3Completed· 131 enrolled
Drug / intervention
efgartigimod +1 morebiological
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04188379
NCT04188379Phase 3Completed

A Phase 3, Multicenter, Randomized, Double-Blinded, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Efgartigimod (ARGX 113) 10 mg/kg Intravenous in Adult Patients With Primary Immune Thrombocytopenia

argenx·interventional·Posted Dec 5, 2019·Updated Mar 13, 2025

In Brief

A Phase 3 clinical trial evaluating efgartigimod and Placebo for Primary Immune Thrombocytopenia. Completed, enrolled 131 participants across 121 sites in 18 countries.

Detailed Summary

This is a randomized, double-blind placebo-controlled multicenter phase 3 trial to evaluate the efficacy and safety of ARGX-113 in participants with primary ITP.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustria, Belgium, Bulgaria, Czechia, France, Georgia, Germany, Hungary, Italy, Japan, Netherlands, Poland, Russia, Spain, Turkey (Türkiye), Ukraine, United Kingdom, United States
Collaborators--

Timeline

Phase 3CompletedFinished
2020202120222023202420252026
First PostedDec 5, 2019
Enrollment StartDec 16, 2019
Primary CompletionFeb 3, 2022
TodayJul 2, 2026
Enrollment to primary: 2.1 yearsPosted 6.6 years ago

Interventions

efgartigimodbiological

Intravenous infusion of efgartigimod

Placeboother

Intravenous infusion of placebo