CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 75 enrolled
Drug / intervention
Maralixibat +1 moredrug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04524390
NCT04524390Phase 2Completed

Randomized, Double-Blind, Placebo-Controlled Phase 2 Study to Evaluate the Efficacy and Safety of Maralixibat in the Treatment of Subjects With Biliary Atresia After Hepatoportoenterostomy

Mirum Pharmaceuticals, Inc.·interventional·Posted Aug 24, 2020·Updated Mar 19, 2025

In Brief

A Phase 2 clinical trial evaluating Maralixibat and Placebo for Biliary Atresia. Completed, enrolled 75 participants across 22 sites in 8 countries.

Detailed Summary

A study to evaluate the efficacy and safety of maralixibat in infants with Biliary Atresia (BA) after Hepatoportoenterostomy (HPE, also known as the Kasai procedure).

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsBiliary Atresia
CountriesChina, Germany, Poland, Singapore, Taiwan, United Kingdom, United States, Vietnam
Collaborators--

Timeline

Phase 2CompletedFinished
202120222023202420252026
First PostedAug 24, 2020
Enrollment StartJul 8, 2021
Primary CompletionNov 7, 2023
Study CompletionFeb 7, 2024
TodayJul 2, 2026
Enrollment to primary: 2.3 yearsPosted 5.9 years ago

Interventions

Maralixibatdrug

A small molecule inhibitor of the ileal bile acid transporter (IBAT)

Placeboother

Identical to maralixibat except for the active drug substance