CI

At a glance

ClinicalIndex Comparison Record
Phase 3Completed· 146 enrolled
Drug / intervention
Vatiquinone +1 moredrug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04577352
NCT04577352Phase 3Completed

A Randomized, Parallel-Arm, Double-Blind, Placebo-Controlled Study With Open-Label Extension to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Friedreich Ataxia (MOVE-FA)

PTC Therapeutics·interventional·Posted Oct 6, 2020·Updated Apr 13, 2026

In Brief

A Phase 3 clinical trial evaluating Vatiquinone and Placebo for Friedreich Ataxia. Completed, enrolled 146 participants across 14 sites in 9 countries.

Detailed Summary

The primary objective of the study is to evaluate the efficacy (using the modified Friedreich Ataxia Rating Scale \[mFARS\]) and safety of vatiquinone in participants with Friedreich ataxia (FA).

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustralia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain, United States
Collaborators--

Timeline

Phase 3CompletedFinished
202120222023202420252026
First PostedOct 6, 2020
Enrollment StartDec 17, 2020
Primary CompletionApr 4, 2023
Study CompletionOct 2, 2023
TodayJul 2, 2026
Enrollment to primary: 2.3 yearsPosted 5.7 years ago

Interventions

Vatiquinonedrug

Vatiquinone will be administered per dose and schedule specified in the arm.

Placebodrug

Placebo will be administered per schedule specified in the arm.