CI

At a glance

ClinicalIndex Comparison Record
Phase 2Recruiting· 296 target
Drug / intervention
Axatilimabdrug
Likely dose
Not stated in record
Key inclusion· 6
  • Age ≥2 years at informed consent
  • Allogeneic HSCT recipients with active cGVHD requiring systemic immune suppression per 2014 NIH criteria
  • Refractory or recurrent active cGVHD despite ≥2 prior lines of systemic therapy
  • Adequate organ and bone marrow functions within 14 days of randomization
Key exclusion· 14
  • Acute GVHD without cGVHD manifestations
  • Evidence of relapse of underlying cancer or post-transplant lymphoproliferative disease at screening
  • History of acute or chronic pancreatitis
  • History of myositis

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04710576
NCT04710576Phase 2RecruitingUpdate OverdueCompletion was 38mo ago
Enrollment Stalled
Long Recruiting
Update Overdue

AGAVE-201, A Phase 2, Open-label, Randomized, Multicenter Study to Evaluate the Efficacy, Safety and Tolerability of Axatilimab at 3 Different Doses in Patients With Recurrent or Refractory Active Chronic Graft Versus Host Disease Who Have Received at Least 2 Lines of Systemic Therapy

Syndax Pharmaceuticals·interventional·Posted Jan 14, 2021·Updated Jun 16, 2026

In Brief

A Phase 2 clinical trial evaluating Axatilimab for Chronic Graft-versus-host-disease. Currently recruiting, targeting 296 participants across 121 sites in 16 countries.

Signals

Enrollment appears stalled

Detailed Summary

This is a Phase 2 study to evaluate the efficacy, safety, and tolerability of axatilimab at 3 different dose levels in participants with recurrent or refractory active chronic graft versus host disease (cGVHD) who have received at least 2 prior lines of systemic therapy.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustralia, Belgium, Canada, France, Germany, Greece, Israel, Italy, Poland, Portugal, Singapore, South Korea, Spain, Taiwan, United Kingdom, United States
Collaborators--

Timeline

Phase 2Recruiting
2021202220232024202520262027
First PostedJan 14, 2021
Enrollment StartMar 4, 2021
Primary CompletionApr 7, 2023
Study CompletionSep 1, 2027
TodayJul 2, 2026
Enrollment to primary: 2.1 yearsPosted 5.5 years ago

Interventions

Axatilimabdrug

Axatilimab is a high-affinity antibody targeting the colony stimulating factor 1 receptor (CSF-1R). CSF-1R signaling has been demonstrated in nonclinical studies to be the key regulatory pathway involved in the expansion and infiltration of donor-derived macrophages that mediate the disease processes involved in cGVHD.