CI

At a glance

ClinicalIndex Comparison Record
N/ARecruiting· 700 target
Drug / intervention
Not specified
Likely dose
Not stated in record
Key inclusion· 3
  • Symptom onset before age 18 years
  • Age under 30 years
  • Genetically confirmed HSP variant or relative of confirmed case
Key exclusion· 1
  • Lack of HSP diagnosis and/or no relation to individual with confirmed diagnosis

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04712812
NCT04712812N/ARecruitingOn TrackUpdated 3mo ago
Long Recruiting

Registry and Natural History Study for Early Onset Hereditary Spastic Paraplegia (HSP)

Boston Children's Hospital·observational·Posted Jan 15, 2021·Updated Mar 18, 2026

In Brief

An observational study for Hereditary Spastic Paraplegia and 10 related conditions. Currently recruiting, targeting 700 participants across 1 site.

Detailed Summary

The Registry and Natural History Study for Early Onset Hereditary Spastic Paraplegia (HSP) is focused on gathering longitudinal clinical data as well as biological samples (skin and/or blood and/or saliva) from male and female patients, under the age of 30, who exhibited early onset symptoms of HSP with (1) a clinical diagnosis of hereditary spastic paraplegia and (2) the presence of variants in HSP related genes and/or be a relative of a person with such a diagnosis. Currently, the treatment for this disorder is generally symptomatic and available therapies improve quality of life, but are grossly inefficient in slowing the disease progression. Access to the registry information will be limited to the study staff who are responsible for recruitment and maintenance of the registry. We hope that recruitment into the registry for studies will advance knowledge of the causes, clinical course, diagnosis, and treatment of these conditions.

Study Details

Study Typeobservational
Allocation--
Masking--
Primary Purpose--
CountriesUnited States
Collaborators--

Timeline

N/ARecruiting
20212022202320242025202620272028202920302031
First PostedJan 15, 2021
Enrollment StartApr 27, 2020
Primary CompletionDec 31, 2030
TodayJul 2, 2026
Enrollment to primary: 10.7 yearsPosted 5.5 years agoPrimary completion in 4.5 years