CI

At a glance

ClinicalIndex Comparison Record
Phase 3Completed· 804 enrolled
Drug / intervention
Simufilam +1 moredrug
Likely dose
Simufilam 100 mgfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04994483
NCT04994483Phase 3Completed

A Phase 3, Randomized, Double-blind, Placebo-controlled, Parallel-group, 52-week Study Evaluating the Safety and Efficacy of Simufilam 100 mg Tablets in Subjects With Mild-to-Moderate Alzheimer's Disease

Cassava Sciences, Inc.·interventional·Posted Aug 6, 2021·Updated May 25, 2025

In Brief

A Phase 3 clinical trial evaluating Simufilam and Placebo for Alzheimer Disease. Completed, enrolled 804 participants across 88 sites in 3 countries.

Detailed Summary

A 52-week safety and efficacy study of simufilam (PTI-125) given twice daily to participants with mild-to-moderate Alzheimer's disease (AD) for 52 weeks. Approximately 750 participants will be randomized (1:1) to receive either placebo or 100 mg tablets of simufilam, twice daily, for 52 weeks. Clinic visits will occur 4 weeks after the baseline visit, and then every 12 weeks until the end of the study. The safety of simufilam, and its efficacy in enhancing cognition and slowing cognitive and functional decline will be evaluated.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustralia, Canada, United States
CollaboratorsPremier Research

Timeline

Phase 3CompletedFinished
20222023202420252026
First PostedAug 6, 2021
Enrollment StartNov 3, 2021
Primary CompletionOct 2, 2024
TodayJul 2, 2026
Enrollment to primary: 2.9 yearsPosted 4.9 years ago

Interventions

Simufilamdrug

Simufilam is a novel drug candidate designed to treat and slow the progression of AD. Simufilam binds with femtomolar affinity to an altered conformation of filamin A that is present in the brain of patients with AD and critical to the toxicity of Aβ42. In this study, simufilam will be given b.i.d. for 52 weeks at a dose of 100 mg.

Placebodrug

Matching placebo given b.i.d. for 52 weeks.