CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 12 enrolled
Drug / intervention
Pegcetacoplandrug
Likely dose
Pegcetacoplan 1080 mgfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT05148299
NCT05148299Phase 2Completed

An Open-label, Single-arm, Multicenter Pilot Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Efficacy and Safety of Pegcetacoplan in Patients With Transplant-associated Thrombotic Microangiopathy (TA-TMA) After Hematopoietic Stem Cell Transplantation (HSCT)

Swedish Orphan Biovitrum·interventional·Posted Dec 8, 2021·Updated Nov 28, 2025

In Brief

A Phase 2 clinical trial evaluating Pegcetacoplan for Transplant-Associated Thrombotic Microangiopathy. Completed, enrolled 12 participants across 14 sites in 5 countries.

Detailed Summary

The purpose of the study was to assess pharmacokinetics (PK), pharmacodynamics (PD), efficacy, and safety of pegcetacoplan in patients with TA-TMA after HSCT.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesFrance, Greece, Italy, Spain, United States

Timeline

Phase 2CompletedFinished
20222023202420252026
First PostedDec 8, 2021
Enrollment StartFeb 1, 2022
Primary CompletionDec 8, 2024
TodayJul 2, 2026
Enrollment to primary: 2.9 yearsPosted 4.6 years ago

Interventions

Pegcetacoplandrug

20-cc glass vials-1080 mg