CI

At a glance

ClinicalIndex Comparison Record
Phase 1Completed· 24 enrolled
Drug / intervention
Agalsidase beta from Biosidus 1 mg/kg +1 morebiological
Likely dose
Agalsidase beta from Biosidus 1 mg/kgfrom record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT05343715
NCT05343715Phase 1Completed

Comparative Pharmacokinetic and Pharmacodynamic Study Between 2 Agalsidase Beta Formulations at a Single Dose of 1 mg/kg of Agalsidase (Biosidus) and Fabrazyme (Sanofi Genzyme) as Intravenous Infusion in Male Healthy Volunteers

Bio Sidus SA·interventional·Posted Apr 25, 2022·Updated Oct 15, 2025

In Brief

A Phase 1 clinical trial evaluating Agalsidase beta from Biosidus 1 mg/kg and Fabrazyme (agalsidase beta) 1 mg/kg for Fabry Disease. Completed, enrolled 24 participants across 1 site.

Detailed Summary

Pharmacokinetic/Pharmacodynamic Study of 2 agalsidase beta Formulations in Single Dose Administered to Healthy Volunteers as intravenous infusion, at a concentration of 1 mg/kg

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsFabry Disease
CountriesArgentina
Collaborators--

Timeline

Phase 1CompletedFinished
20222023202420252026
First PostedApr 25, 2022
Enrollment StartOct 23, 2021
Primary CompletionMar 6, 2022
Study CompletionApr 17, 2022
TodayJul 2, 2026
Enrollment to primary: 4 monthsPosted 4.2 years ago

Interventions

Agalsidase beta from Biosidus 1 mg/kgbiological

Patients received an infusion of 1 mg/kg of Agalsidase Beta from Biosidus. Final infusion dose is achieved with lyophilized drug at concentration 35 mg and 5 mg

Fabrazyme (agalsidase beta) 1 mg/kgbiological

Patients received an infusion of 1 mg/kg of Fabrazyme. Final infusion dose is achieved with lyophilized drug at concentration 35 mg and 5 mg