CI

At a glance

ClinicalIndex Comparison Record
Phase 3Active· 29 enrolled
Drug / intervention
Berotralstatdrug
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT05453968
NCT05453968Phase 3Active

A Phase 3 Study to Evaluate the Safety and Pharmacokinetics of Berotralstat Prophylaxis in Children With Hereditary Angioedema Who Are 2 to < 12 Years of Age

BioCryst Pharmaceuticals·interventional·Posted Jul 12, 2022·Updated Feb 25, 2026

In Brief

A Phase 3 clinical trial evaluating Berotralstat for Hereditary Angioedema and Pediatric. Active but no longer recruiting, targeting 29 participants across 15 sites in 10 countries.

Detailed Summary

The purpose of this study is to evaluate the pharmacokinetics (PK), safety and effectiveness of berotralstat to determine the appropriate weight-based dose for pediatric participants 2 to \< 12 years of age for prophylactic treatment to prevent attacks of hereditary angioedema (HAE).

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesAustria, Canada, France, Germany, Israel, Italy, Poland, Romania, Spain, United Kingdom
Collaborators--

Timeline

Phase 3Active
20232024202520262027
First PostedJul 12, 2022
Enrollment StartOct 25, 2022
Primary CompletionSep 11, 2024
Study CompletionFeb 1, 2027
TodayJul 2, 2026
Enrollment to primary: 1.9 yearsPosted 4.0 years ago

Interventions

Berotralstatdrug

Administered orally once daily