CI

At a glance

ClinicalIndex Comparison Record
Phase 3Recruiting· 510 target
Drug / intervention
Dordaviprone (ONC201) +2 moredrug
Likely dose
Dordaviprone (ONC201) 625 mgfrom record
Key inclusion· 10
  • Histologically confirmed H3 K27M-mutant diffuse glioma (new diagnosis)
  • Body weight ≥10 kg at randomization
  • K27M mutation detected by IHC or NGS in CLIA-certified laboratory
  • Contrast-enhanced brain MRI prior to radiotherapy (post-resection if surgery performed)
Key exclusion· 18
  • Primary spinal tumor
  • Diffuse intrinsic pontine glioma (DIPG)
  • Leptomeningeal spread or cerebrospinal fluid dissemination
  • Concurrent malignancy

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT05580562
NCT05580562Phase 3RecruitingOn TrackUpdated 2mo ago
Long Recruiting

ONC201 for the Treatment of Newly Diagnosed H3 K27M-mutant Diffuse Glioma Following Completion of Radiotherapy: A Randomized, Double-Blind, Placebo-Controlled, Multicenter Study

Jazz Pharmaceuticals·interventional·Posted Oct 14, 2022·Updated Apr 16, 2026

In Brief

A Phase 3 clinical trial evaluating Dordaviprone (ONC201), Dordaviprone (ONC201) + Placebo, and 1 other intervention for H3 K27M and Glioma. Currently recruiting, targeting 510 participants across 162 sites in 18 countries.

Detailed Summary

This is a randomized, double-blind, placebo-controlled, parallel-group, international, Phase 3 study in patients with newly diagnosed H3 K27M-mutant diffuse glioma to assess whether treatment with dordaviprone (ONC201) following frontline radiotherapy will extend overall survival and progression-free survival in this population. Eligible participants will have histologically diagnosed H3 K27M-mutant diffuse glioma and have completed standard frontline radiotherapy.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
ConditionsH3 K27M, Glioma
CountriesArgentina, Australia, Austria, Brazil, Canada, Denmark, Germany, Hong Kong, Israel, Italy, Japan, Netherlands, Singapore, South Korea, Spain, Switzerland, United Kingdom, United States
CollaboratorsChimerix, Inc.

Timeline

Phase 3Recruiting
202320242025202620272028
First PostedOct 14, 2022
Enrollment StartJan 23, 2023
Primary CompletionJun 1, 2028
TodayJul 2, 2026
Enrollment to primary: 5.4 yearsPosted 3.7 years agoPrimary completion in 1.9 years

Interventions

Dordaviprone (ONC201)drug

Participants ≥ 52.5 kg will receive 625 mg of dordaviprone (5 × 125-mg capsules) dosing days; participants \< 52.5 kg will receive a dose (and corresponding number of capsules) scaled by body weight and rounded to 125-mg increments.

Dordaviprone (ONC201) + Placebodrug

Participants ≥ 52.5 kg will receive 625 mg of dordaviprone (5 × 125-mg capsules) or matching placebo on dosing days; participants \< 52.5 kg will receive a dose (and corresponding number of capsules) scaled by body weight and rounded to 125-mg increments

Placeboother

Participants will receive placebo (same number of capsules as the dordaviprone dose) on dosing days