CI

At a glance

ClinicalIndex Comparison Record
Phase 2Completed· 14 enrolled
Drug / intervention
AAV-GAD Low Dose +2 moregenetic
Likely dose
Not stated in record
Structured eligibility isn't available for this trial yet — see the full criteria in the Eligibility tab below.

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT05603312
NCT05603312Phase 2Completed

A Randomized, Double-Blind, Sham-Controlled Study to Evaluate the Safety and Tolerability of Glutamic Acid Decarboxylase Gene Transfer to the Subthalamic Nuclei in Participants With Parkinson's Disease

MeiraGTx, LLC·interventional·Posted Nov 2, 2022·Updated Sep 5, 2025

In Brief

A Phase 2 clinical trial evaluating AAV-GAD Low Dose, AAV-GAD High Dose, and 1 other intervention for Parkinson's Disease. Completed, enrolled 14 participants across 6 sites.

Detailed Summary

The objective of this clinical trial was to evaluate the safety and tolerability of adeno-associated virus (AAV)-mediated delivery of glutamic acid decarboxylase (GAD) gene transfer into the subthalamic nuclei (STN) of participants with Parkinson's Disease.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesUnited States
Collaborators--

Timeline

Phase 2CompletedFinished
2023202420252026
First PostedNov 2, 2022
Enrollment StartOct 5, 2022
Primary CompletionSep 6, 2024
TodayJul 2, 2026
Enrollment to primary: 1.9 yearsPosted 3.7 years ago

Interventions

AAV-GAD Low Dosegenetic

Bilateral infusion of AAV-GAD low dose

AAV-GAD High Dosegenetic

Bilateral infusion of AAV-GAD high dose

Sham Surgeryprocedure

Sham infusion